Abstract

The invention provides compounds, compositions and methods for treating myotonic dystrophy. The compounds can selectively bind to CUG repeats in RNA, or to CTG repeats in DNA, and inhibit replication of the nucleic acids.
Original languageEnglish (US)
U.S. patent number8754084
StatePublished - Jun 17 2014

Fingerprint

Dive into the research topics of 'Therapeutic methods and agents for treating myotonic dystrophy'. Together they form a unique fingerprint.

Cite this