Abstract
The invention provides compounds, compositions and methods for treating myotonic dystrophy. The compounds can selectively bind to CUG repeats in RNA, or to CTG repeats in DNA, and inhibit replication of the nucleic acids.
| Original language | English (US) |
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| U.S. patent number | 8754084 |
| Filing date | 3/27/13 |
| State | Published - Jun 17 2014 |