20062020

Research output per year

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Research Output

Treatment of a Mouse Model of ALS by In Vivo Base Editing

Lim, C. K. W., Gapinske, M., Brooks, A. K., Woods, W. S., Powell, J. E., Zeballos C., M. A., Winter, J., Perez-Pinera, P. & Gaj, T., Jan 1 2020, (Accepted/In press) In : Molecular Therapy.

Research output: Contribution to journalArticle

  • CRISPR-Cas9-Mediated Genome Editing Increases Lifespan and Improves Motor Deficits in a Huntington's Disease Mouse Model

    Ekman, F. K., Ojala, D. S., Adil, M. M., Lopez, P. A., Schaffer, D. V. & Gaj, T., Sep 6 2019, In : Molecular Therapy - Nucleic Acids. 17, p. 829-839 11 p.

    Research output: Contribution to journalArticle

    Open Access
  • A Hypothalamic Switch for REM and Non-REM Sleep

    Chen, K. S., Xu, M., Zhang, Z., Chang, W. C., Gaj, T., Schaffer, D. V. & Dan, Y., Mar 7 2018, In : Neuron. 97, 5, p. 1168-1176.e4

    Research output: Contribution to journalArticle

  • hPSC-Derived Striatal Cells Generated Using a Scalable 3D Hydrogel Promote Recovery in a Huntington Disease Mouse Model

    Adil, M. M., Gaj, T., Rao, A. T., Kulkarni, R. U., Fuentes, C. M., Ramadoss, G. N., Ekman, F. K., Miller, E. W. & Schaffer, D. V., May 8 2018, In : Stem Cell Reports. 10, 5, p. 1481-1491 11 p.

    Research output: Contribution to journalArticle

  • Innovations in CRISPR technology

    Brooks, A. K. & Gaj, T., Aug 2018, In : Current Opinion in Biotechnology. 52, p. 95-101 7 p.

    Research output: Contribution to journalReview article